Sequence-Selective Translation Inhibition as a Novel, Proximity-Based Small Molecule Therapeutic Modality

  • Drug-like small-molecule, sequence-selective interdiction of disease associated protein synthesis
  • Addressing highly validated yet historically undruggable targets in oncology and neurodegeneration
  • Strong reliance on machine learning fueled by biophysical characterization, cryo-EM, ribosome profiling and genomics